News: 2007
06-Dec-2007
PTC Therapeutics Announces Additional $1.6 Million Grant from the Spinal Muscular Atrophy Foundation South Plainfield, NJ – December 6, 2007 – PTC Therapeutics, Inc. (PTC), a biopharmaceutical company focused on the discovery, development, and commercialization of small-molecule drugs targeting post-transcriptional control mechanisms, today announced an expanded research collaboration with the Spinal Muscular Atrophy (SMA) Foundation.read more »
06-Nov-2007
SMA Summit on Drug Development in Neurology TodayNeurology Today: SMA Drug Development Gains Momentum Under NINDS Model for Neuro-Research Partnerships. Reprinted with permission from the American Academy of Neurology from Neurology Today, Nov. 6, 2007.
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19-Oct-2007
Nationwide Grassroots Call to Action To Urge Your Representative and Senators To Cosponsor The SMA Treatment Acceleration Act We would like to extend our heartfelt gratitude to the many SMA families, researchers and friends who have already joined our Nationwide Call to Action in support of The SMA Treatment Acceleration Act! We are writing to ask for your continued help and ACTION in support of this important legislation.read more »
10-Oct-2007
SMA Organizations Representatives Visit Capitol Hill to Thank Sponsors of the SMA Treatment Acceleration Act October 10, 2007 - Cynthia Joyce, Executive Director of the SMA Foundation, along with Martha Slay, President of FightSMA and Kenneth Hobby, Executive Director of Families of SMA recently visited on Capitol Hill...read more »
02-Oct-2007
Raising Awareness for Children with SMAThe SMA Foundation warmly thank Megan and Shea Megale for all their efforts in raising awareness for children living with SMA.
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18-Sep-2007
Spinal Muscular Atrophy Foundation and BG Medicine Announce CollaborationNew York, NY and Waltham, MA – September 18, 2007 – The Spinal Muscular Atrophy Foundation and BG Medicine today announced a collaboration to discover plasma biomarkers of drug efficacy for spinal muscular atrophy (SMA), the leading genetic cause of mortality in infants and toddlers. This project seeks to discover a clinically-useful molecular biomarker, which can then be used to monitor the efficacy of potential drugs in clinical trials.
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12-Sep-2007
The "SMA Treatment Acceleration Act" Was Introduced in the U.S. Senate by Stabenow (D-MI) and Isakson (R-GA) September 12, 2007 - The SMA Community is very pleased to announce that legislation to enhance federal support for Spinal Muscular Atrophy (SMA) research, S.2042, “The SMA Treatment Acceleration Act” has been introduced today...read more »
03-Aug-2007
The "SMA Treatment Acceleration Act" Was Introduced in the U.S. House of Representatives by Kennedy (D-RI) and Cantor (R-VA)August 3, 2007 - We are very pleased to announce that legislation to enhance federal support for Spinal Muscular Atrophy (SMA) research, H.R. 3334, "The SMA Treatment Acceleration Act," has been introduced today...
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22-Jun-2007
Families of Spinal Muscular Atrophy Announces Major Breakthrough in Development of Drug Candidate for Currently Untreatable DiseaseCongratulations to Families of SMA on the selection of the first novel clinical candidate for SMA.
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29-Mar-2007
NIH/NINDS Director Highlights Remarkable Scientific Advances in SMA Research in Congressional HearingWashington, D.C. – March 29, 2007 – In Senate Subcommittee on Labor-HHS-Education Appropriations hearings this week, National Institute of Neurological Disorders and Stroke Director, Story C. Landis Ph.D., testified on the remarkable scientific advances that...
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20-Mar-2007
Treatment Extends Survival in SMA Mouse - Researchers are Optimistic About HDAC InhibitorsReprinted with permission from the American Academy of Neurology from the March 6, 2007 issue of Neurology Today, pages 26-27.
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13-Mar-2007
Cold Spring Harbor Laboratory Shows Correcting RNA Splicing May Help Treat Spinal Muscular AtrophyThe SMA Foundation congratulates investigator Adrian Krainer on his latest publication. (Posted March 13, 2007).
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02-Mar-2007
SMA Investigator's Research Highlighted in Science.The SMA Foundation congratulates investigator Giorgio Battaglia on the recent recognition of his work. (Posted March 2, 2007).
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22-Feb-2007
Treatment Extends Survival in Mouse Model of Spinal Muscular Atrophy.The SMA Foundation congratulates Scientific Advisory Board Members Kenneth Fischbeck, MD and Charlotte Sumner, MD on their latest publication.
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11-Jan-2007
SMA Investigator Receives 2006 MacArthur 'Genius' Award.The SMA Foundation congratulates Kevin Eggan, PhD, Assistant Professor, Harvard University and Principal Investigator, Harvard Stem Cell Institute, on being named a MacArthur Fellow. Dr. Eggan is currently developing SMA cell lines from human stem cells. Click here to find out more about the Eggan Lab. (Posted January 11, 2007).
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