The Biomarkers for Spinal Muscular Atrophy (BforSMA) clinical trial is a current pilot study looking to identify potential biomarkers (measures) that can be used to evaluate SMA disease severity and future treatments. Recruitment is ongoing and as of January 29, 2009, 71 subjects have been recruited from 18 clinical sites in the United States and Canada. An additional 49 SMA patients between the ages of 2 and 12 are needed for the study and we hope to close enrollment soon. We are looking for SMA families within driving distance of the clinical sites to participate in this one day study. For more information about the BforSMA study and for a list of enrolling sites, please click here.
For more information on other SMA trials and the International SMA Patient Registry is recruiting for, please see the press release below.